Tuberous Sclerosis
Clinical trial pipeline · Data from ClinicalTrials.gov
See which Tuberous Sclerosis trials may be worth asking aboutClinical trial pipeline · Data from ClinicalTrials.gov
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This is a multinational, open-label, single-arm trial of adjunctive SVG103 (paxalisib) treatment in adults with FCD-II, TSC, and HME.
Tuberous sclerosis is a rare, hereditary disease in which patients develop multiple tumors. Although not cancerous, the tumors can affect various organs, includ…
Pulmonary lymphangioleiomyomatosis (LAM) is a destructive lung disease typically affecting women of childbearing age. Currently, there is no effective therapy f…
There are currently no approved medications for the treatment of anxiety in children and youth with neurodevelopmental disorders (NDDs), both common and rare. S…
This study is designed to evaluate the genetics involved in the development of lung disease by surveying genes involved in the process of breathing and examinin…
The clinical trial is intended to assess for clinical evidence of Clemastine Fumarate as a myelin repair therapy in patients with chronic inflammatory injury-ca…
The purpose of this study is to characterize the developmental phenotype of ASD and ID and to identify biomarkers using advanced MRI methodology and electrophys…
This study will monitor for potential chronic liver injury and liver fibrosis, in participants treated with cannabidiol oral solution.