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Propionic/Methylmalonic Acidemias
Clinical trial pipeline · Data from ClinicalTrials.gov
See which Propionic/Methylmalonic Acidemias trials may be worth asking aboutClinical trial pipeline · Data from ClinicalTrials.gov
See which Propionic/Methylmalonic Acidemias trials may be worth asking aboutNorth America
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To obtain short-term and long-term clinical safety information, in pediatric and adult patients with PA and MMA treated with Carbaglu®.
This is a prospective mixed-design study focused on the long-term management of propionic aciduria (PA) and methylmalonic aciduria (MMA) with N-carbamylglutamat…
Newborn screening (NBS) is a global initiative of systematic testing at birth to identify babies with pre-defined severe but treatable conditions. With a simple…
Early Check provides voluntary screening of newborns for a selected panel of conditions. The study has three main objectives: 1) develop and implement an approa…