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Inherited Hematological Diseases
Clinical trial pipeline · Data from ClinicalTrials.gov
See which Inherited Hematological Diseases trials may be worth asking aboutClinical trial pipeline · Data from ClinicalTrials.gov
See which Inherited Hematological Diseases trials may be worth asking aboutNorth America
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Trials may have sites in multiple countries. Filtering shows any trial with at least one site in the selected country.
Prolonged activated partial thromboplastin time (APTT) is a frequent laboratory finding that may reflect a broad spectrum of underlying conditions, ranging from…
Background: Chronic granulomatous disease (CGD) is a rare immune disorder caused by a mutation in the CYBB gene. People with CGD have white blood cells that do…
Background: Fanconi anemia (FA) is a rare, inherited cancer syndrome. FA causes a range of physical issues. Children with FA may have abnormal features; these…
This study will evaluate patients with abnormal immune function that results in recurrent or unusual infections or chronic inflammation. This may include inheri…
This study is conducted to confirm whether etavopivat works well at reducing the number of Vaso-occlusive crisis VOCs (sickle cell pain crises) caused by obstru…
The purpose of this study is to evaluate what effect, if any, mismatched unrelated volunteer donor and/or haploidentical related donor stem cell transplant may…
The collection of human specimens from both patients and healthy volunteers is necessary for the development of laboratory assays to further basic and clinical…
This study will test how well a new medicine called concizumab works for participants who have haemophilia A or B with or without inhibitors. The purpose is to…