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Hereditary Ataxia
Clinical trial pipeline · Data from ClinicalTrials.gov
See which Hereditary Ataxia trials may be worth asking aboutClinical trial pipeline · Data from ClinicalTrials.gov
See which Hereditary Ataxia trials may be worth asking aboutNorth America
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The main goal of the project is provision of a global registry for mitochondrial disorders to harmonize previous national registries, enable world-wide particip…
Spinocerebellar ataxias (SCA) are genetic neurological diseases that cause imbalance, poor coordination, and speech difficulties. There are different kinds of S…
This clinical trial is evaluating a drug called ART0380 in participants with advanced or metastatic solid tumors. The main goals of this study are to: * Find t…
This is a phase 1b, first in-human, open-label, dose-finding study investigating the safety and tolerability of SGT-212 in participants with Friedreich's ataxia…
Friedreich's ataxia (FRDA) is an autosomal recessive disease characterized by loss of coordination and cardiomyopathy. It is the most common form of inherited a…
The purpose of Study LX2006-03, a multicenter, Phase 2, open-label, randomized, controlled study, is to evaluate the efficacy and safety of LX2006 gene therapy…
The purpose of this study is to confirm the treatment effects of vatiquinone on the key measures of FA disease progression.
Work participation is essential for quality of life, providing purpose, social interaction, financial security, and shaping social status. Work participation is…