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Wolfram Syndrome 1
Clinical trial pipeline · Data from ClinicalTrials.gov
See which Wolfram Syndrome 1 trials you may qualify forClinical trial pipeline · Data from ClinicalTrials.gov
See which Wolfram Syndrome 1 trials you may qualify forIn this study, the investigators hypothesize that studying monogenic variants with strong effect associated with severe insulin deficiency of Wolfram syndrome w…
The study has two aims: 1. To (1a) determine the frequency of monogenic diabetes misdiagnosed as type 1 diabetes (T1D) and (2) to define an algorithm for case…
This trial aims to investigate the efficacy, safety and tolerability of sodium valproate in the treatment of patients with Wolfram syndrome. 70 paediatric and a…
This study is an open label Phase II study to evaluate the safety and efficacy of AMX0035 in adults with Wolfram syndrome.
All patients with Wolfram syndrome and recessive optic atrophy due to a mutation of the WFS1 from a single Center were included in a retrospective study. Evolut…