Type 1 Facioscapulohumeral Muscular Dystrophy
Clinical trial pipeline · Data from ClinicalTrials.gov
See which Type 1 Facioscapulohumeral Muscular Dystrophy trials may be worth asking aboutClinical trial pipeline · Data from ClinicalTrials.gov
See which Type 1 Facioscapulohumeral Muscular Dystrophy trials may be worth asking aboutNorth America
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The goal of this study is to investigate the effects of personalized exercise treatment on dynamic balance and physical function in comparison with regular foll…
A Randomized, Double-blind, Placebo-controlled, Phase 3 Study to Evaluate the Efficacy and Safety of Intravenous AOC 1020 for the Treatment of Facioscapulohumer…
The purpose of this study is to evaluate the safety, tolerability, pharmacokinetics (PK) and pharmacodynamics (PD) of ARO-DUX4 in participants with facioscapulo…
Myotonic dystrophy (DM) and facioscapulohumeral muscular dystrophy (FSHD) are inherited disorders characterized by progressive muscle weakness and loss of muscl…
The ActiLiège-Adult study is a prospective, longitudinal, observational study designed to collect natural history data on adult patients with neurological or me…
The data to be collected is intended to help healthcare providers make important medical and financial decisions concerning FSHD1, through an enhanced understan…
A Phase 2 Open-label Extension Study to Evaluate the Long-Term Safety, Tolerability, and Efficacy of AOC 1020 Administered Intravenously to Participants with Fa…
A Randomized, Double-blind, Placebo-controlled, Phase 1/2 Study to Evaluate the Safety, Tolerability, Pharmacokinetics, Pharmacodynamics, and Exploratory Effica…