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Trifunctional Protein Deficiency
Clinical trial pipeline · Data from ClinicalTrials.gov
See which Trifunctional Protein Deficiency trials you may qualify forClinical trial pipeline · Data from ClinicalTrials.gov
See which Trifunctional Protein Deficiency trials you may qualify forExpanded access may be provided for qualified patients who have limited treatment options and are not eligible for a clinical trial.
The main goal of this study is to evaluate the effects of triheptanoin versus Medium-chain Triglycerides (MCT) on frequency of Major Clinical Events (MCEs).
The primary objective of this study is to assess the long-term safety, including pregnancy, infant, and lactation outcomes, of patients with LC-FAOD who are enr…