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Transthyretin Familial Amyloidosis Polyneuropathy (TTR-FAP)
Clinical trial pipeline · Data from ClinicalTrials.gov
See which Transthyretin Familial Amyloidosis Polyneuropathy (TTR-FAP) trials may be worth asking aboutClinical trial pipeline · Data from ClinicalTrials.gov
See which Transthyretin Familial Amyloidosis Polyneuropathy (TTR-FAP) trials may be worth asking aboutNorth America
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Transthyretin amyloidosis (ATTR) is a disease where the normally occurring transthyretin (TTR) protein falls apart and forms amyloid, a sticky plaque-like subst…
Approximately 1.5 million of the 44 million Blacks in the United States are carriers of the valine-to-isoleucine substitution at position 122 (V122I) in the tra…
The MaesTTRo study aims to enroll a global cohort of patients with transthyretin (ATTR) amyloidosis to longitudinally observe the natural course of the disease…
The purpose of this study is to: * Describe epidemiological and clinical characteristics, natural history and real-world clinical management of ATTR amyloidosi…
This study will be conducted to evaluate the efficacy and safety of a single dose of nexiguran ziclumeran (NTLA-2001) compared to placebo in participants with A…
The goal of this clinical trial is to investigate whether new imaging techniques can help us to better understand the cardiac amyloidosis. The disease can be sl…
The aim of this observational cohort study is to characterise use of eplontersen in patients with prior liver transplant or with pre-existing severe hepatic imp…
This is a multicenter observational study consisting of retrospective and prospective phases. The retrospective phase will entail secondary data collection from…