Skeletal Abnormalities
Clinical trial pipeline · Data from ClinicalTrials.gov
See which Skeletal Abnormalities trials may be worth asking aboutClinical trial pipeline · Data from ClinicalTrials.gov
See which Skeletal Abnormalities trials may be worth asking aboutNorth America
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The purpose of this study is to better understand the natural history, clinical outcomes, and biological features of Gaucher disease in patients receiving stand…
This is a multicenter, multinational, randomized, active-controlled, operationally seamless Phase 2/3 study of BMN 333 in treatment-naïve pediatric participants…
Background: There are 461 conditions that affect the bones (skeletal disorders). Many of these are not well understood and do not have any specific treatments.…
This is a long-term, multicenter, non-interventional study of children ages 2.5 to \<17 years with hypochondroplasia (HCH).
This is a Phase 2, multicenter, randomized, placebo-controlled study to evaluate the safety and efficacy of infigratinib in participants \< 3 years old with ACH…
The purpose of this research study is to determine the potential of a multiparametric ultrasound approach to non-invasively monitor disease progression and to s…
Groundbreaking cardiac surgery has significantly improved survival rates for patients with single-chamber hearts. However, despite these life-saving interventio…
This prospective clinical trial aims to evaluate the clinical and radiographic outcomes of the low sagittal medial ramus osteotomy-a technical modification of t…