PGM1-CDG - Phosphoglucomutase 1-Related Congenital Disorder of Glycosylation

Clinical trial pipeline · Data from ClinicalTrials.gov

See which PGM1-CDG - Phosphoglucomutase 1-Related Congenital Disorder of Glycosylation trials you may qualify for

Total trials

Actively recruiting

Phase 3 trials

Completed

Trial phase breakdown

Trial status

All recent trials (2 shown)

Not Yet RecruitingPhase 2

NCT05402332

Evaluating the Efficacy and Safety of D-galactose in PGM1-CDG (AVTX-801)

This is a clinical trial to evaluate the efficacy of AVTX-801 (D-galactose) on the clinical manifestations of PGM1-CDG in participants currently taking D-galact…

United States8 participantsStarted 2026-10-01

Treatment: AVTX-801, Placebo

UnknownPhase 1/2

NCT03404856

Study of ORL-1G (D-galactose) in Patients With Glycogen Storage Disease Type 14

Study of ORL-1G in Patients With Glycogen Storage Disease Type 14

Turkey (Türkiye)5 participantsStarted 2017-10-31

Treatment: ORL-1G - D-galactose