UnknownPhase 1/2

Study of ORL-1G (D-galactose) in Patients With Glycogen Storage Disease Type 14

Turkey (Türkiye)5 participantsStarted 2017-10-31

Plain-language summary

Study of ORL-1G in Patients With Glycogen Storage Disease Type 14

Who can participate

Age range18 Years

SexALL

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AI-rewrites the medical criteria so a patient or caregiver can understand them. Always confirm with the trial site.

Inclusion Criteria: * Diagnosis of Glycogen Storage Disease Type 14. * Less than 18 years old. Exclusion Criteria: * Diagnosis of any other disease that is not a manifestation of Glycogen Storage Disease Type 14.

What they're measuring

Improvement in liver function.

Timeframe: 3 months after treatment starts

Trial details

NCT IDNCT03404856

SponsorOrpha Labs

Sponsor typeINDUSTRY

Study typeINTERVENTIONAL

Primary completion2019-10-31

Contact for this trial

Study Coordinator Study Coordinator

+90 537 763 6241 business.development@orphalabs.com

View on ClinicalTrials.gov More Glycogen Storage Disease, Type 14 trials