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Peroxisome Biogenesis Disorders
Clinical trial pipeline · Data from ClinicalTrials.gov
See which Peroxisome Biogenesis Disorders trials may be worth asking aboutClinical trial pipeline · Data from ClinicalTrials.gov
See which Peroxisome Biogenesis Disorders trials may be worth asking aboutNorth America
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A series of N-of-1, crossover, randomized, placebo-controlled, double-blinded trial. Hydroxychloroquine (HCQ) and a crossover to placebo (order is randomized an…
The PBD are a rare group of inherited disorders due to the failure to form functional cellular peroxisomes. Most patients have progressive hearing and visual lo…