Mucopolysaccharidosis IV Type A
Clinical trial pipeline · Data from ClinicalTrials.gov
See which Mucopolysaccharidosis IV Type A trials may be worth asking aboutClinical trial pipeline · Data from ClinicalTrials.gov
See which Mucopolysaccharidosis IV Type A trials may be worth asking aboutNorth America
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Morquio A disease is a devastating systemic skeletal disease in which detailed progression and pathogenesis remain unknown. The proposed project aims to establi…
The purpose of this study is to better understand how heart and blood vessel problems develop in people with Mucopolysaccharidosis (MPS). The investigators are…
There are relatively few data available on type II collagen disorders, and evidence is lacking on the disease course in relation to symptoms and development of…
ScreenPlus is a consented, multi-disorder pilot newborn screening program implemented in conjunction with the New York State Newborn Screening Program that prov…
Early Check provides voluntary screening of newborns for a selected panel of conditions. The study has three main objectives: 1) develop and implement an approa…