Long Chain Fatty Acid Oxidation Disorders
Clinical trial pipeline · Data from ClinicalTrials.gov
See which Long Chain Fatty Acid Oxidation Disorders trials you may qualify forClinical trial pipeline · Data from ClinicalTrials.gov
See which Long Chain Fatty Acid Oxidation Disorders trials you may qualify forIn this study, the exercise tolerance in patients with long-chain fatty acid oxidation disorders (LcFAOD) will be compared to that of healthy volunteers who are…
Ammonia is a waste product of protein and amino acid catabolism and is also a potent neurotoxin. High blood ammonia levels on the brain can manifest as cytotoxi…
Expanded access may be provided for qualified patients who have limited treatment options and are not eligible for a clinical trial.
The main goal of this study is to evaluate the effects of triheptanoin versus Medium-chain Triglycerides (MCT) on frequency of Major Clinical Events (MCEs).
The primary objective of this study is to assess the long-term safety, including pregnancy, infant, and lactation outcomes, of patients with LC-FAOD who are enr…