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LGMDR9
Clinical trial pipeline · Data from ClinicalTrials.gov
See which LGMDR9 trials you may qualify forClinical trial pipeline · Data from ClinicalTrials.gov
See which LGMDR9 trials you may qualify forThe purpose of this study is to evaluate the safety and tolerability of a single intravenous infusion of AB-1003 in adults diagnosed with limb girdle muscular d…
This is a 24-month, observational study of up to 1000 participants with Limb Girdle Muscular Dystrophy (LGMD), Myotonic Dystrophy Type 2 (DM2), and late onset P…
The Congenital Muscle Disease Patient and Proxy Reported Outcome Study (CMDPROS) is a longitudinal 10 year study to identify and trend care parameters, adverse…
Prospective, longitudinal, interventional, single-group, multicenter natural history study to better know the LGMD2I disease physiopathology. The duration of pa…
Phase 1 dose escalation study to assess tolerability and safety of ATA-100 with 5-year follow-up
This study will evaluate the safety and efficacy of long-term administration of BBP-418 in patients with LGMD2I/R9. The study will include patients ages 12 to 6…