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Late Infantile Metachromatic Leukodystrophy
Clinical trial pipeline · Data from ClinicalTrials.gov
See which Late Infantile Metachromatic Leukodystrophy trials may be worth asking aboutClinical trial pipeline · Data from ClinicalTrials.gov
See which Late Infantile Metachromatic Leukodystrophy trials may be worth asking aboutNorth America
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The main aim of the study is to determine if SHP611 given by injection into the spinal fluid that surrounds the brain and spinal cord (intrathecal; IT) prolongs…
There is currently no effective treatment for late infantile MLD once clinical symptoms are evident. METAZYM is a recombinant human arylsulfatase A developed fo…