Glycogen Storage Disease Type 1 (GSD 1)

Clinical trial pipeline · Data from ClinicalTrials.gov

See which Glycogen Storage Disease Type 1 (GSD 1) trials you may qualify for

Total trials

Actively recruiting

Phase 3 trials

Completed

Trial phase breakdown

Trial status

Actively recruiting — 1 trial

RecruitingNot Applicable

NCT06795152

Rare Glycogen Storage Diseases Natural History Study

The purpose of this study is to collect and study key medical data about several ultra-rare GSDs (Glycogen Storage Diseases) including, but not limited to, GSD…

United States200 participantsStarted 2024-12-23

Treatment: No intervention

All recent trials (5 shown)

TerminatedPhase 1/2

NCT04990388

Safety, Tolerability, and Pharmacokinetics of UX053 in Patients With Glycogen Storage Disease Type III (GSD III)

The primary objective of the study is to evaluate the safety of UX053 in adults with Glycogen Storage Disease Type III (GSD III).

United States, Italy9 participantsStarted 2021-10-18

Treatment: UX053, Placebo

TerminatedNot Applicable

NCT05196165

Clinical Survey Study to Assess Physical Function and the Incidence of Hypoglycemia in Participants With Glycogen Storag…

The primary objective of this study is to evaluate the incidence of hypoglycemia in adult and pediatric participants with glycogen storage disease type III (GSD…

United States, Netherlands14 participantsStarted 2022-05-20

Treatment: No Intervention

Glycogen Storage Disease Type 1 (GSD 1)

Trial phase breakdown

Trial status

Actively recruiting — 1 trial

Rare Glycogen Storage Diseases Natural History Study

All recent trials (5 shown)

Safety, Tolerability, and Pharmacokinetics of UX053 in Patients With Glycogen Storage Disease Type III (GSD III)

Clinical Survey Study to Assess Physical Function and the Incidence of Hypoglycemia in Participants With Glycogen Storag…

Trial phase breakdown

Trial status

Actively recruiting — 1 trial

Rare Glycogen Storage Diseases Natural History Study

All recent trials (5 shown)

Safety, Tolerability, and Pharmacokinetics of UX053 in Patients With Glycogen Storage Disease Type III (GSD III)

Clinical Survey Study to Assess Physical Function and the Incidence of Hypoglycemia in Participants With Glycogen Storag…

Study of ORL-1G (D-galactose) in Patients With Glycogen Storage Disease Type 14

Overnight Feeding Study in Glycogen Storage Disease Type 1