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Friedreich's Ataxia (FA)
Clinical trial pipeline · Data from ClinicalTrials.gov
See which Friedreich's Ataxia (FA) trials may be worth asking aboutClinical trial pipeline · Data from ClinicalTrials.gov
See which Friedreich's Ataxia (FA) trials may be worth asking aboutNorth America
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This is a phase 1b, first in-human, open-label, dose-finding study investigating the safety and tolerability of SGT-212 in participants with Friedreich's ataxia…
The purpose of Study LX2006-03, a multicenter, Phase 2, open-label, randomized, controlled study, is to evaluate the efficacy and safety of LX2006 gene therapy…
Characteristics and clinical course of disease In participants with cardiomyopathy associated with Friedreich Ataxia (CLARITY-FA)
The purpose of this study is to confirm the treatment effects of vatiquinone on the key measures of FA disease progression.
The goal of this study is to obtain gamma-aminobutyric acid (GABA) and glutathione (GSH) assessment derived from magnetic resonance spectroscopy (MRS), to be us…