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Duchene Muscular Dystrophy
Clinical trial pipeline · Data from ClinicalTrials.gov
See which Duchene Muscular Dystrophy trials you may qualify forClinical trial pipeline · Data from ClinicalTrials.gov
See which Duchene Muscular Dystrophy trials you may qualify forThis open-label extension study aims to evaluate the long-term safety and tolerability of weekly BMN 351 infusions, as well as to assess the effect of BMN 351 o…
The purpose of this research study is to determine the potential of a multiparametric ultrasound approach to non-invasively monitor disease progression and to s…
25 boys, ages ranging from 6 to 16 years, diagnosed with Duchene's muscular Dystrophy (DMD) will participated in the study. They will be selected from the Pedia…