Evaluation of Brain Dysfunction in Patients with Duchene Muscular Dystrophy (NCT06732011) | Clinical Trial Compass
Not Yet RecruitingNot Applicable
Evaluation of Brain Dysfunction in Patients with Duchene Muscular Dystrophy
42 participantsStarted 2024-12-30
Plain-language summary
To study the cognitive function \& psychiatric aspects of patients with DMD by specific psychometry tests \& its relation to quality of life of the patients To evaluate brain structural changes using MRI and correlate them to the cognitive \& psychiatric manifestations of the patients To correlate the cognitive function with the neurophysiological tests and imaging done to the patient
Who can participate
Age range
5 Years – 18 Years
Sex
MALE
See this in plain English?
AI-rewrites the medical criteria so a patient or caregiver can understand them. Always confirm with the trial site.
Inclusion Criteria:
\- Male patients Age children \& adolescent (5-18yrs) Patients diagnosed \& genetically confirmed DMD, with cross matching of healthy subjects of the same age and number
Exclusion Criteria:
Medical or neurological condition affecting cognition (as endocrinal as Diabetes Mellitus \& hypothyroidism, autoimmune disease, history of brain trauma, birth asphyxia, neonatal jaundice, …..) Surgical condition that could potentially impact cognitive function Patients of other types of muscular dystrophy Those who refuse to participate in the study Those with sensory disability (as hearing loss, blindness, severe speech delay) Those with non-invasive or invasive ventilation support with inability to speak and answer oral questions
Questions worth asking your doctor
Bring these to your next appointment. They're a starting point for a shared conversation — not a sign you qualify or a recommendation to enrol.
1Based on my diagnosis and history, is this trial worth exploring for me — or is there a standard treatment we should try first?
2What does this trial's phase tell us about how much is already known about its safety and benefit?
3What would taking part actually involve for me — visits, tests, time, and travel?
4What are the known and possible risks or side effects I should weigh, and how would they be monitored?
5If this trial isn't the right fit, what other options or trials would you suggest I look into?
Generated to help you prepare — always confirm anything about your own eligibility and care with the study team and your doctor.
Questions for the trial coordinator
The trial coordinator is the person who runs the study day to day. These cover the practical side — logistics, costs, and what taking part would actually mean for your life. The study team confirms whether you meet the criteria; these are questions to ask, not a sign you qualify.
1What does taking part actually involve week to week — how many visits, where, and how long does each one take?
2What costs are covered by the study, and what might I have to pay for myself, including travel, parking, or time off work?
3What happens during screening, and what happens if the study team confirms I don't meet the criteria after those tests?
4Who pays for the scans, blood work, and other tests the trial requires — the study, my insurance, or me?
5How will being in the trial affect my regular care, and will my own doctor stay informed and involved?
6Can I leave the trial at any point if I change my mind, and what would happen to my care if I do?
A starting point for the conversation — always confirm anything about your own eligibility, costs, and care with the study team and your doctor.