Calpain-3 Deficiency Limb Girdle Muscular Dystrophy Type 2A
Clinical trial pipeline · Data from ClinicalTrials.gov
See which Calpain-3 Deficiency Limb Girdle Muscular Dystrophy Type 2A trials you may qualify forClinical trial pipeline · Data from ClinicalTrials.gov
See which Calpain-3 Deficiency Limb Girdle Muscular Dystrophy Type 2A trials you may qualify forThe purpose of this study is to evaluate the safety and tolerability of a single intravenous infusion of AB-1003 in adults diagnosed with limb girdle muscular d…
This is a 24-month, observational study of up to 1000 participants with Limb Girdle Muscular Dystrophy (LGMD), Myotonic Dystrophy Type 2 (DM2), and late onset P…
This is a 24-month, observational study of 100 participants with Limb Girdle Muscular Dystrophy type R1, also known as CAPN3.
Limb girdle muscular dystrophies were originally defined as a postnatal progressive muscle disease, which begins and primarily affects the pelvic and scapular m…
This is an observational study, no drug (marketed or investigational) will be provided as part of the study, and the study procedures will have no impact on the…
Limb-girdle muscular dystrophies (LGMD) are a series of rare progressive genetic disorders that are characterized by wasting and weakness of the voluntary proxi…