Alpha and Beta Thalassemia
Clinical trial pipeline · Data from ClinicalTrials.gov
See which Alpha and Beta Thalassemia trials you may qualify forClinical trial pipeline · Data from ClinicalTrials.gov
See which Alpha and Beta Thalassemia trials you may qualify forBackground: Blood disorders like sickle cell disease and malaria affect many people around the world. Researchers want to learn more about blood disorders. To…
This is a phase II, open-label, prospective study of T cell receptor alpha/beta depletion (TCR α/β TCD) peripheral blood stem cell (PBSC) transplantation for ch…
This is a data collection study that will examine the general diagnostic and treatment data associated with the reduced-intensity chemotherapy-based regimen pai…
The objective of this study is to evaluate the efficacy of using a reduced-intensity condition (RIC) regimen with umbilical cord blood transplant (UCBT), double…
Children, adolescents, and young adults with malignant and non-malignant conditionsundergoing an allogeneic stem cell transplantation (AlloSCT) will have the st…
This is an international prospective registry of patients with Alpha thalassemia to understand the natural history of the disease and the outcomes of fetal ther…
The primary purpose of this study was to compare the effect of mitapivat versus placebo on hemolytic anemia in participants with alpha- or beta-non-transfusion…
The primary objective of this study was to compare the effect of mitapivat versus placebo on transfusion burden in participants with α- or β-transfusion-depende…