The goal of this observational study is to investigate whether the type, location, and extent of pathogenic variants in the DMD gene are associated with cardiac dysfunction in male children, adolescents, and young adults with dystrophinopathies. The study also evaluates whether cardiac biomarkers and electrocardiographic findings can facilitate the early identification of cardiac involvement. Participants will undergo electrocardiography, blood sampling for cardiac biomarker assessment, and transthoracic echocardiography, with cardiac dysfunction evaluated using ejection fraction (EF) and global longitudinal strain (GLS).
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Correlation between pathogenic DMD gene variants and left ventricular ejection fraction (EF)
Timeframe: On the day of the baseline assessment
Correlation between pathogenic DMD gene variants and global longitudinal strain (GLS)
Timeframe: On the day of the baseline assessment
Correlation between pathogenic DMD gene variants and blood levels of high-sensitivity troponin T (hs-TnT)
Timeframe: On the day of the baseline assessment
Correlation between pathogenic DMD gene variants and blood levels of N-terminal pro-brain natriuretic peptide (NT-proBNP)
Timeframe: On the day of the baseline assessment