By InvitationNot Applicable

Effect of Enzyme Replacement Therapy on Cardiac Function in Children With Gaucher Disease Type 3

Egypt44 participantsStarted 2024-04-01

Plain-language summary

all cases confirmed diagnosis of Gaucher disease type 3 recieving enzyme replacement therapy at Assiut university hospital

Who can participate

SexALL

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AI-rewrites the medical criteria so a patient or caregiver can understand them. Always confirm with the trial site.

Inclusion Criteria: * Any sex * No age limit * Gaucher disease type 3 * Receiving enzyme replacement therapy Exclusion Criteria: * Age18 years old * Cases of gaucher type 1 and 2 * Other lipid storage disease

What they're measuring

Evaluate Pulmonary Hypertension (PH) in Egyptian GD Type 3 Patients

Timeframe: 6 months

Evaluate Valvular Involvement in Egyptian GD Type 3 Patients

Timeframe: 6 months

Trial details

NCT IDNCT06627543

SponsorNoha Osman

Sponsor typeOTHER

Study typeOBSERVATIONAL

Primary completion2025-01-01

View on ClinicalTrials.gov More Gaucher Disease Type 3 trials