Active — Not RecruitingNot Applicable

Long-term Follow-up Study of Patients Who Received hLB-001 Gene Therapy

United States4 participantsStarted 2022-07-15

Plain-language summary

This is a non-interventional long-term follow-up study of patients who have participated in LogicBio studies for the treatment of MMA and received hLB-001

Who can participate

Age range18 Years

SexALL

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Inclusion Criteria: * Participant has previously participated in a LogicBio clinical trial and received hLB-001. Exclusion Criteria: * None

What they're measuring

Incidence of treatment emergent adverse events

Timeframe: 15 years

Trial details

NCT IDNCT05506254

SponsorAlexion Pharmaceuticals, Inc.

Sponsor typeINDUSTRY

Study typeOBSERVATIONAL

Primary completion2037-01-01

View on ClinicalTrials.gov More Methylmalonic Acidemia trials