CompletedNot Applicable

Pyruvate Kinase Deficiency Global Longitudinal Registry Substudy of Protocol AG348-C-008

United States, Italy, Netherlands13 participantsStarted 2021-07-02

Plain-language summary

This is a substudy of Study AG348-C-008, an observational, longitudinal, multicenter, global registry that aims to better understand the longitudinal clinical implications of pyruvate kinase deficiency (PK deficiency). The primary purpose of this study is to describe the cognition of participants with PK deficiency, as objectively measured by the Cogstate Brief Battery (CBB).

Who can participate

Age range18 Years

SexALL

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Inclusion Criteria: * Participant must be ≥18 years of age; * Participant must be enrolled in Study AG348-C-008.

What they're measuring

Change Over Time in Cogstate Brief Battery (CBB) Scores

Timeframe: Day 0, Day 90

Trial details

NCT IDNCT04995315

SponsorAgios Pharmaceuticals, Inc.

Sponsor typeINDUSTRY

Study typeOBSERVATIONAL

Primary completion2023-09-22

View on ClinicalTrials.gov More Pyruvate Kinase Deficiency trials