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Variant Late-Infantile Neuronal Ceroid Lipofuscinosis
Clinical trial pipeline · Data from ClinicalTrials.gov
See which Variant Late-Infantile Neuronal Ceroid Lipofuscinosis trials may be worth asking aboutClinical trial pipeline · Data from ClinicalTrials.gov
See which Variant Late-Infantile Neuronal Ceroid Lipofuscinosis trials may be worth asking aboutNorth America
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The goal of this clinical trial is to learn if a gene therapy called scAAV9.CB.CLN6 can treat children with CLN6 Batten disease (variant late infantile neuronal…
This is a phase 1/2, open-label, single dose study to evaluate the safety and efficacy of AT-GTX-501 delivered intrathecally into the lumbar spinal cord region…