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Variant Late-Infantile Neuronal Ceroid Lipofuscinosis
Clinical trial pipeline · Data from ClinicalTrials.gov
See which Variant Late-Infantile Neuronal Ceroid Lipofuscinosis trials you may qualify forClinical trial pipeline · Data from ClinicalTrials.gov
See which Variant Late-Infantile Neuronal Ceroid Lipofuscinosis trials you may qualify forThis is a phase 1/2, open-label, single dose study to evaluate the safety and efficacy of AT-GTX-501 delivered intrathecally into the lumbar spinal cord region…
This is a multicenter, international, study to assess the natural history data from people with Batten disease by collecting both retrospective and prospective…