Telomere Biology Disorders With Bone Marrow Failure
Clinical trial pipeline · Data from ClinicalTrials.gov
See which Telomere Biology Disorders With Bone Marrow Failure trials may be worth asking aboutClinical trial pipeline · Data from ClinicalTrials.gov
See which Telomere Biology Disorders With Bone Marrow Failure trials may be worth asking aboutNorth America
Europe
Asia-Pacific
Rest of World
Trials may have sites in multiple countries. Filtering shows any trial with at least one site in the selected country.
The purpose of this study is to see if a vitamin-like substance called quercetin is safe for people who have a rare condition called Dyskeratosis congenita (DC)…
The goal of this clinical trial is to learn if a combination therapy of deoxycytidine (dC) plus deoxythymidine (dT) is safe in patients with telomere biology di…
This is a phase II trial of T cell receptor alpha/beta depletion (α/β TCD) peripheral blood stem cell (PBSC) transplantation in patients with inherited bone mar…
This is a Phase I/II, open label, single center study to assess the safety and tolerability of EXG34217 in bone marrow failure patients with telomere biology di…
This is a long-term rollover follow-up study for Phase I/II study (Protocol EXG-US-01).