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Spinocerebellar Ataxia 27B (SCA27B)
Clinical trial pipeline · Data from ClinicalTrials.gov
See which Spinocerebellar Ataxia 27B (SCA27B) trials you may qualify forClinical trial pipeline · Data from ClinicalTrials.gov
See which Spinocerebellar Ataxia 27B (SCA27B) trials you may qualify forThis international, multi-center, multi-modal, and prospective observational cohort study aims to validate trial outcomes for capturing disease progression in S…
Spinocerebellar ataxias 27B (SCA27B) is caused by an expansion of ≥ 250 GAA triplets in the FGF14 gene and accounts for 15% of cerebellar ataxias (around 500 pa…