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RUNX1 Familial Platelet Disorder
Clinical trial pipeline · Data from ClinicalTrials.gov
See which RUNX1 Familial Platelet Disorder trials may be worth asking aboutClinical trial pipeline · Data from ClinicalTrials.gov
See which RUNX1 Familial Platelet Disorder trials may be worth asking aboutNorth America
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Background: Genes tell the body and its cells how to work. Familial platelet disease (FPD) or FPD with associated malignancies (FPDMM) is caused by a variant i…
Background: Runt-related transcription factor 1 (RUNX1) gene regulates the formation of blood cells. People with mutations of this gene may bleed or bruise eas…
To evaluate the safety and feasibility of collecting hematopoietic stem cells (HSC) in participants with RUNX1-FPD.