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Rett Syndrome
Clinical trial pipeline · Data from ClinicalTrials.gov
See which Rett Syndrome trials may be worth asking aboutClinical trial pipeline · Data from ClinicalTrials.gov
See which Rett Syndrome trials may be worth asking aboutNorth America
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Assessing cognitive functions among individuals with severe intellectual and developmental disabilities (IDD), including RTT, is often challenging due to floor…
The primary objectives of this study are to evaluate the safety, tolerability and preliminary efficacy of a single intrathecal (IT) dose of TSHA-102 in pediatri…
This observational research study is designed to learn more about how the brain processes sound in individuals with Rett syndrome. Participants will complete a…
The RETT REVOLUTION trial is a placebo-controlled, single-blinded, exploratory study with patients serving as their own control ("N of 1" trial design) where th…
Primary Objective • To investigate the efficacy of treatment with oral Bionetide versus placebo in girls and women with Rett syndrome Key Secondary Objective…
This observational study evaluates functional and developmental outcomes in pediatric participants undergoing a two week intensive multimodal neurorehabilitatio…
The purpose of this study is to investigate the efficacy of fenfluramine hydrochloride (HCl) versus placebo in study participants with Rett syndrome (RTT).
This study will evaluate the efficacy and safety profiles of the investigational gene therapy, NGN-401, in females with typical Rett syndrome.