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RETT Syndrome With Proven MECP2 Mutation
Clinical trial pipeline · Data from ClinicalTrials.gov
See which RETT Syndrome With Proven MECP2 Mutation trials you may qualify forClinical trial pipeline · Data from ClinicalTrials.gov
See which RETT Syndrome With Proven MECP2 Mutation trials you may qualify forThis observational study evaluates functional and developmental outcomes in pediatric participants undergoing a two week intensive multimodal neurorehabilitatio…
Rett Syndrome (RTT) is a rare neurodevelopmental disorder caused by an MECP2 gene mutation on the X chromosome, primarily affecting females. It causes progressi…
Based on our clinical observations, many girls with RETT syndrome, a severe neuro-developmental encephalopathy, suffer from osteoporosis which can appear at a v…
The FENRTT2 study will investigate the efficacy and safety of a medicinal cannabis plant extract with extremely low THC (delta-9-tetrahydrocannabinol), NTI164,…
Study Brief Summary overall design This study explored dose escalation of single-arm, open, single intrathecal injection in female RTT subjects with MECP2 gene…