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Propionic Acidemia (PA) , Methylmalonic Acidemia (MMA)
Clinical trial pipeline · Data from ClinicalTrials.gov
See which Propionic Acidemia (PA) , Methylmalonic Acidemia (MMA) trials you may qualify forClinical trial pipeline · Data from ClinicalTrials.gov
See which Propionic Acidemia (PA) , Methylmalonic Acidemia (MMA) trials you may qualify forEvaluate the Long Term Effectiveness \& Safety of the use of Carglumic Acid (Carbaglu®) in Patients with Propionic Acidemia (PA) or Methylmalonic Acidemia (MMA)…
Longitudinal, exploratory, natural history study of patients with MMA due to mut deficiency and PA to characterize the changes in blood disease biomarkers over…
The overall objective of this drug trial is to determine whether the treatment of acute hyperammonemia with N-carbamyl-L-glutamate (NCG, Carglumic acid) in prop…