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Propionic Acidemia (PA) , Methylmalonic Acidemia (MMA)
Clinical trial pipeline · Data from ClinicalTrials.gov
See which Propionic Acidemia (PA) , Methylmalonic Acidemia (MMA) trials may be worth asking aboutClinical trial pipeline · Data from ClinicalTrials.gov
See which Propionic Acidemia (PA) , Methylmalonic Acidemia (MMA) trials may be worth asking aboutNorth America
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Evaluate the Long Term Effectiveness \& Safety of the use of Carglumic Acid (Carbaglu®) in Patients with Propionic Acidemia (PA) or Methylmalonic Acidemia (MMA)…
Longitudinal, exploratory, natural history study of patients with MMA due to mut deficiency and PA to characterize the changes in blood disease biomarkers over…