Phenylalanine Hydroxylase Deficiencies

Clinical trial pipeline · Data from ClinicalTrials.gov

See which Phenylalanine Hydroxylase Deficiencies trials you may qualify for

Total trials

Actively recruiting

Phase 3 trials

Completed

Trial phase breakdown

Trial status

All recent trials (1 shown)

TerminatedPhase 2/3

NCT00432822

Long-Term Tetrahydrobiopterin Treatment in PKU Patients of 0-18 Years - Study on Phenylalanine Tolerance and Safety

The aim of the study is to confirm the efficacy and safety of BH4 in the treatment of hyperphenylalaninemia caused by phenylalanine hydroxylase deficiency in pa…

Location not specified50 participants

Treatment: tetrahydrobiopterin (BH4)