Pediatric SDLT CNS Disorders

Clinical trial pipeline · Data from ClinicalTrials.gov

See which Pediatric SDLT CNS Disorders trials you may qualify for

Total trials

Actively recruiting

Phase 3 trials

Completed

Trial phase breakdown

Trial status

All recent trials (1 shown)

Active — Not RecruitingPhase 1/2

NCT07410143

Investigation of Individualised Antisense Oligonucleotides (ASOs) in People With Unique Genetic Variants Causing Severel…

This study is being conducted to evaluate individualised antisense oligonucleotides (ASOs) in participants with severely debilitating, life threatening (SDLT) c…

United Kingdom1 participantsStarted 2026-01-13

Treatment: Individualized ASO