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Pediatric Pyruvate Kinase Deficiency
Clinical trial pipeline · Data from ClinicalTrials.gov
See which Pediatric Pyruvate Kinase Deficiency trials you may qualify forClinical trial pipeline · Data from ClinicalTrials.gov
See which Pediatric Pyruvate Kinase Deficiency trials you may qualify forACTIVATE-KidsT (AG348-C-022) is a multicenter study designed to evaluate the efficacy and safety of treatment with mitapivat compared with placebo in pediatric…
Study ACTIVATE-Kids (AG348-C-023) will evaluate the efficacy and safety of orally administered mitapivat as compared with placebo in pediatric participants with…
This is an open-label Phase I trial to evaluate the safety of a hematopoietic cell-based gene therapy for patients with Pyruvate Kinase Deficiency (PKD).