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Paroxysmal Nocturnal Hemoglobinuria (PNH)
Clinical trial pipeline · Data from ClinicalTrials.gov
See which Paroxysmal Nocturnal Hemoglobinuria (PNH) trials may be worth asking aboutClinical trial pipeline · Data from ClinicalTrials.gov
See which Paroxysmal Nocturnal Hemoglobinuria (PNH) trials may be worth asking aboutNorth America
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As part of a post-approval commitment, the Korean health authority requests a study to characterize safety and effectiveness in patients who are treated with Da…
The purpose of this study is to evaluate the safety, effectiveness, and biological activity (how the investigational medication is processed by the body) of peg…
This is a post-marketing surveillance study conducted as part of the Risk Management Plan (RMP) for South Korea, to evaluate the safety and effectiveness of ipt…
This study evaluates iptacopan effectiveness and safety in routine clinical practice, with a focus on hematological response, transfusion avoidance, and patient…
Background: * Stem cell transplants from related donors (allogenic stem cell transplants) can be used to treat individuals with certain kinds of severe blood d…
This study is researching a treatment combination with two experimental drugs called pozelimab and cemdisiran referred to as "study drugs". Researchers are look…
Examine red and white blood cells of PNH patients with bone marrow failure syndromes.
This is an observational single-arm descriptive cohort study based on the secondary use of data collected on iptacopan-treated patients with paroxysmal nocturna…