Neutral Lipid Storage Disease

Clinical trial pipeline · Data from ClinicalTrials.gov

See which Neutral Lipid Storage Disease trials you may qualify for

Total trials

Actively recruiting

Phase 3 trials

Completed

Trial phase breakdown

Trial status

Actively recruiting — 1 trial

RecruitingNot Applicable

NCT02918032

International Registry Study of Neutral Lipid Storage Disease (NLSD) / Triglyceride Deposit Cardiomyovasculopathy (TGCV)…

This study aims to understand the state of onset of NLSD(neutral lipid storage disease) / TGCV(triglyceride deposit cardiovasculopathy) worldwide, background in…

United States, Austria +2 more120 participantsStarted 2014-01

All recent trials (6 shown)

TerminatedPhase 2

NCT02193867

Clinical Study In Infants With Rapidly Progressive Lysosomal Acid Lipase Deficiency

This was an open-label, repeat-dose, study of sebelipase alfa in infants with rapidly progressive lysosomal acid lipase deficiency (LAL-D). Eligible participant…

United States, Finland +2 more10 participantsStarted 2014-06-06

Treatment: Sebelipase Alfa

UnknownNot Applicable

NCT02635269

Fat and Sugar Metabolism During Exercise in Patients With Metabolic Myopathy

This study aims to characterize the pathophysiological mechanisms of 21 different metabolic myopathies. The study will focus on exercise capacity and the metabo…

Denmark60 participantsStarted 2016-01

Treatment: Sugar

Neutral Lipid Storage Disease

Trial phase breakdown

Trial status

Actively recruiting — 1 trial

International Registry Study of Neutral Lipid Storage Disease (NLSD) / Triglyceride Deposit Cardiomyovasculopathy (TGCV)…

All recent trials (6 shown)

Clinical Study In Infants With Rapidly Progressive Lysosomal Acid Lipase Deficiency

Fat and Sugar Metabolism During Exercise in Patients With Metabolic Myopathy

Trial phase breakdown

Trial status

Actively recruiting — 1 trial

International Registry Study of Neutral Lipid Storage Disease (NLSD) / Triglyceride Deposit Cardiomyovasculopathy (TGCV)…

All recent trials (6 shown)

Clinical Study In Infants With Rapidly Progressive Lysosomal Acid Lipase Deficiency

Fat and Sugar Metabolism During Exercise in Patients With Metabolic Myopathy

Clinical Study on the Safety of CNT-02 for TGCV and NLSD-M

Safety, Tolerability, Efficacy, Pharmacokinetics, and Pharmacodynamics of Sebelipase Alfa in Children With Growth Failur…

The Effect of Fibrate Therapy in Two Patients With Neutral Lipid Storage Disease With Myopathy (NLSDM)