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Neurodegeneration With Brain Iron Accumulation (NBIA)
Clinical trial pipeline · Data from ClinicalTrials.gov
See which Neurodegeneration With Brain Iron Accumulation (NBIA) trials you may qualify forClinical trial pipeline · Data from ClinicalTrials.gov
See which Neurodegeneration With Brain Iron Accumulation (NBIA) trials you may qualify forTIRCON-reg aims to * continue the provision of a global registry and natural history study for NBIA disorders * harmonize and cover existing national and singl…
MARKERS-NDD is a prospective, observational, longitudinal study, which aims to collect data from patients affected by neurodegenerative diseases (NDD) followed…
The purpose of this study is to learn more about how people with the condition pantothenate kinase-associated neurodegeneration (PKAN) respond to a specialized…
Rares diseases are a heterogeneous group of conditions which need important tools for diagnosis. The use of high-throughput sequencing is able to diagnose half…
This trial is a multicenter, unblinded, single-arm pilot study, lasting one year (plus one year extension Amendment n.3 25 August 2009, plus two years follow-up…