Mucopolysaccharidosis Type IH (MPS IH, Hurler Syndrome)
Clinical trial pipeline · Data from ClinicalTrials.gov
See which Mucopolysaccharidosis Type IH (MPS IH, Hurler Syndrome) trials may be worth asking aboutClinical trial pipeline · Data from ClinicalTrials.gov
See which Mucopolysaccharidosis Type IH (MPS IH, Hurler Syndrome) trials may be worth asking aboutNorth America
Europe
Asia-Pacific
Rest of World
Trials may have sites in multiple countries. Filtering shows any trial with at least one site in the selected country.
A multi-center randomized clinical trial to compare OTL-203 (gene therapy) with stem cell transplant (standard of care) in patients with MPS-IH (Hurler syndrome…
This is a prospective, observational multicenter study to collect blood from patients with mucopolysaccharidosis type IH undergoing laronidase therapy and a ste…