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Mucopolysaccharidosis Type IH (MPS IH, Hurler Syndrome)
Clinical trial pipeline · Data from ClinicalTrials.gov
See which Mucopolysaccharidosis Type IH (MPS IH, Hurler Syndrome) trials you may qualify forClinical trial pipeline · Data from ClinicalTrials.gov
See which Mucopolysaccharidosis Type IH (MPS IH, Hurler Syndrome) trials you may qualify forA multi-center randomized clinical trial to compare OTL-203 (gene therapy) with stem cell transplant (standard of care) in patients with MPS-IH (Hurler syndrome…
This is a prospective, observational multicenter study to collect blood from patients with mucopolysaccharidosis type IH undergoing laronidase therapy and a ste…