Mucopolysaccharidosis Type 3 B

Clinical trial pipeline · Data from ClinicalTrials.gov

See which Mucopolysaccharidosis Type 3 B trials you may qualify for

Total trials

Actively recruiting

Phase 3 trials

Completed

Trial phase breakdown

Trial status

Actively recruiting — 1 trial

RecruitingPhase 1/2

NCT06488924

An Open-label Phase I/II Study of JR-446 in Mucopolysaccharidosis Type IIIB

A Phase I/ II, open-label study, designed to evaluate the safety and explore efficacy of the study drug in development for the treatment of MPS IIIB patients.

Japan10 participantsStarted 2024-11-05

Treatment: JR-446

All recent trials (23 shown)

By InvitationNot Applicable

NCT05368038

ScreenPlus: A Comprehensive, Flexible, Multi-disorder Newborn Screening Program

ScreenPlus is a consented, multi-disorder pilot newborn screening program implemented in conjunction with the New York State Newborn Screening Program that prov…

United States100,000 participantsStarted 2021-05-10

Treatment: Confirmatory Testing

CompletedNot Applicable

NCT05687474

Baby Detect : Genomic Newborn Screening

Newborn screening (NBS) is a global initiative of systematic testing at birth to identify babies with pre-defined severe but treatable conditions. With a simple…

Belgium6,824 participantsStarted 2022-09-01

Mucopolysaccharidosis Type 3 B

Trial phase breakdown

Trial status

Actively recruiting — 1 trial

An Open-label Phase I/II Study of JR-446 in Mucopolysaccharidosis Type IIIB

All recent trials (23 shown)

ScreenPlus: A Comprehensive, Flexible, Multi-disorder Newborn Screening Program

Baby Detect : Genomic Newborn Screening

Trial phase breakdown

Trial status

Actively recruiting — 1 trial

An Open-label Phase I/II Study of JR-446 in Mucopolysaccharidosis Type IIIB

All recent trials (23 shown)

ScreenPlus: A Comprehensive, Flexible, Multi-disorder Newborn Screening Program

Baby Detect : Genomic Newborn Screening

Early Check: Expanded Screening in Newborns

Safety, Tolerability and Efficacy of ICV AX 250 Treatment in MPS IIIB -OLE

Biomarker for Sanfilippo Type A-B-C-D Disease (BioSanfilippo)

A Treatment Extension Study of Mucopolysaccharidosis Type IIIB

A Prospective Natural History Study of Mucopolysaccharidosis Type IIIB (MPS IIIB)

A Long-term Follow-up Study of Patients With MPS IIIB Treated With ABO-101

Gene Transfer Clinical Trial for Mucopolysaccharidosis (MPS) IIIB

Natural History Study of Patients With Mucopolysaccharidosis Type IIIB (MPS IIIB, Sanfilippo Syndrome Type B)

A Treatment Study of Mucopolysaccharidosis Type IIIB

Natural History of Morquio B and Late-Onset of GM1 Gangliosidosis

A Study of Mucopolysaccharidosis Type IIIB (MPS IIIB)

Intracerebral Gene Therapy in Children With Sanfilippo Type B Syndrome

Neurobehavioral Phenotypes in MPS III

Natural History Study to Characterise the Course of Disease Progression in Participants With Mucopolysaccharidosis Type…

Safety, Pharmacokinetics, and Pharmacodynamics/Efficacy of SBC-103 in Mucopolysaccharidosis III, Type B (MPS IIIB)

A Open Label Study in Previously Studied, SBC-103 Treatment Naïve MPS IIIB Subjects to Investigate the Safety, Pharmacok…

A Retrospective Chart Review of Deceased Patients With Mucopolysaccharidosis Type IIIB

Evaluation of Blood Brain Barrier Integrity and Structural Abnormalities in MPS IIIB Patients Using Multimodal Magnetic…