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MPS IIIB (Sanfilippo Syndrome)
Clinical trial pipeline · Data from ClinicalTrials.gov
See which MPS IIIB (Sanfilippo Syndrome) trials may be worth asking aboutClinical trial pipeline · Data from ClinicalTrials.gov
See which MPS IIIB (Sanfilippo Syndrome) trials may be worth asking aboutNorth America
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The primary objectives of this study are to evaluate the effects of Tralesinidase Alfa (TA) on cognition
ScreenPlus is a consented, multi-disorder pilot newborn screening program implemented in conjunction with the New York State Newborn Screening Program that prov…