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MPS 7
Clinical trial pipeline · Data from ClinicalTrials.gov
See which MPS 7 trials you may qualify forClinical trial pipeline · Data from ClinicalTrials.gov
See which MPS 7 trials you may qualify forThe Phase 3 study will use a novel randomized, intra-subject placebo-controlled, single crossover design, referred to as Blind Start, to evaluate the safety and…
The primary objective of the study is to evaluate the long-term safety of UX003 in subjects with MPS 7.
The primary objective was to evaluate the effect of UX003 treatment in pediatric MPS VII participants less than 5 years of age on safety, tolerability, and effi…