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MPS 7
Clinical trial pipeline · Data from ClinicalTrials.gov
See which MPS 7 trials may be worth asking aboutClinical trial pipeline · Data from ClinicalTrials.gov
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The primary objective of the study is to evaluate the long-term safety of UX003 in subjects with MPS 7.
The Phase 3 study will use a novel randomized, intra-subject placebo-controlled, single crossover design, referred to as Blind Start, to evaluate the safety and…