Limb-Girdle Muscular Dystrophy, Type 2E
Clinical trial pipeline · Data from ClinicalTrials.gov
See which Limb-Girdle Muscular Dystrophy, Type 2E trials you may qualify forClinical trial pipeline · Data from ClinicalTrials.gov
See which Limb-Girdle Muscular Dystrophy, Type 2E trials you may qualify forThis is a 24-month, observational study of up to 1000 participants with Limb Girdle Muscular Dystrophy (LGMD), Myotonic Dystrophy Type 2 (DM2), and late onset P…
The goal of this Natural History Study for Charcot-Marie-Tooth is to acquire, record, and analyze patient-reported data and associated genetic reports, Electron…
This is a multicenter, global study of the effects of a single systemic dose of SRP-9003 on beta-sarcoglycan (β-SG) gene expression in participants with limb-gi…
The primary purpose of this study is to evaluate the safety of SRP-9003 and to quantify expression of β-SG in the skeletal muscle of participants with limb-gird…