LGMD2B

Clinical trial pipeline · Data from ClinicalTrials.gov

See which LGMD2B trials you may qualify for

Total trials

Actively recruiting

Phase 3 trials

Completed

Trial phase breakdown

Trial status

Actively recruiting — 1 trial

RecruitingNot Applicable

NCT05989620

Long-Term Development of Muscular Dystrophy Outcome Assessments

This is a 24-month, observational study of up to 1000 participants with Limb Girdle Muscular Dystrophy (LGMD), Myotonic Dystrophy Type 2 (DM2), and late onset P…

United States1,000 participantsStarted 2023-10-18

All recent trials (11 shown)

TerminatedPhase 1

NCT05906251

A Gene Transfer Study to Evaluate the Safety, Tolerability and Efficacy of SRP-6004 in Ambulatory Participants With Limb…

The primary purpose of this study is to evaluate the safety of SRP-6004 administered by intravenous (IV) infusion in ambulatory participants with LGMD2B/R2 (DYS…

United States2 participantsStarted 2023-05-22

Treatment: SRP-6004

By InvitationNot Applicable

NCT04824040

Clinical, Immunological, Morphological and Genetic Characteristics of Patients With Dysferlinopathy (LGMD R2) in the RF

To evaluate specific characteristics of phenotype, immune status, molecular and genetic as well as morphological characteristics of adult patients with limb-gir…

Russia100 participantsStarted 2020-01-15

LGMD2B

Trial phase breakdown

Trial status

Actively recruiting — 1 trial

Long-Term Development of Muscular Dystrophy Outcome Assessments

All recent trials (11 shown)

A Gene Transfer Study to Evaluate the Safety, Tolerability and Efficacy of SRP-6004 in Ambulatory Participants With Limb…

Clinical, Immunological, Morphological and Genetic Characteristics of Patients With Dysferlinopathy (LGMD R2) in the RF

Trial phase breakdown

Trial status

Actively recruiting — 1 trial

Long-Term Development of Muscular Dystrophy Outcome Assessments

All recent trials (11 shown)

A Gene Transfer Study to Evaluate the Safety, Tolerability and Efficacy of SRP-6004 in Ambulatory Participants With Limb…

Clinical, Immunological, Morphological and Genetic Characteristics of Patients With Dysferlinopathy (LGMD R2) in the RF

Dysferlinopathy Protein in Peripheral Blood Monocytes.

A Multicenter Phenotype-Genotype Analysis of LGMD Patients in China

Evaluate Safety and Biological Activity of ATYR1940 in Participants With Limb Girdle Muscular Dystrophy 2B (LGMD2B) and…

Clinical Outcome Study for Dysferlinopathy

rAAVrh74.MHCK7.DYSF.DV for Treatment of Dysferlinopathies

Proteasomal Inhibition for Patients With Mis-sense Mutated Dysferlin

Deflazacort in Dysferlinopathies

Evaluation of Limb-Girdle Muscular Dystrophy