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Leber Congenital Amaurosis 2
Clinical trial pipeline · Data from ClinicalTrials.gov
See which Leber Congenital Amaurosis 2 trials you may qualify forClinical trial pipeline · Data from ClinicalTrials.gov
See which Leber Congenital Amaurosis 2 trials you may qualify forCoRDS, or the Coordination of Rare Diseases at Sanford, is based at Sanford Research in Sioux Falls, South Dakota. It provides researchers with a centralized, i…
The purpose of the study is to determine whether HG004 as gene therapy is safe and effective for the treatment of Leber Congenital Amaurosis caused by mutations…
This is a Phase 1/2 Study to Assess the Safety and Efficacy of OCU400 in patients with retinitis pigmentosa associated with NR2E3 and RHO mutations and in patie…
The study is a follow-on to a Phase 1 dose-escalation and safety study.
Multi-site, non-randomized, observational study, for up to 15 years after subretinal AAV2-hRPE65v2 administration for each subject. The study is a non-intervent…