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LCA (Leber Congenital Amaurosis)
Clinical trial pipeline · Data from ClinicalTrials.gov
See which LCA (Leber Congenital Amaurosis) trials may be worth asking aboutClinical trial pipeline · Data from ClinicalTrials.gov
See which LCA (Leber Congenital Amaurosis) trials may be worth asking aboutNorth America
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Trials may have sites in multiple countries. Filtering shows any trial with at least one site in the selected country.
The purpose of this double-masked, randomized, placebo-controlled, paired-eye study is to evaluate the efficacy, safety and tolerability of Sepofarsen in subjec…
The purpose of the study is to determine whether HG004 as gene therapy is safe and effective for the treatment of Leber Congenital Amaurosis caused by mutations…
Primary Objective: To evaluate the safety and tolerability of ascending doses of ATSN-101 administered as a unilateral subretinal injection in patients with Le…
A recombinant adeno-associated virus serotype 2 (rAAV2) vector has been altered to carry the human RPE65 (hRPE65) gene. This vector has been shown to restore vi…