Late-infantile Neuronal Ceroid Lipofuscinosis Type 2 (CLN2)
Clinical trial pipeline · Data from ClinicalTrials.gov
See which Late-infantile Neuronal Ceroid Lipofuscinosis Type 2 (CLN2) trials may be worth asking aboutClinical trial pipeline · Data from ClinicalTrials.gov
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This is a multicenter, observational study for patients with a confirmed diagnosis of neuronal ceroid lipofuscinosis type 2 (CLN2 disease), also known as TPP1 d…
This is a phase I/II randomized, masked, clinical trial to determine the safety and efficacy of intravitreal administration of cerliponase alfa.