Lafora Disease

Clinical trial pipeline · Data from ClinicalTrials.gov

See which Lafora Disease trials you may qualify for

Total trials

Actively recruiting

Phase 3 trials

Completed

Trial phase breakdown

Trial status

Actively recruiting — 1 trial

RecruitingPhase 1/2

NCT06609889

A Safety and Efficacy of Intrathecally Administered ION283 in Patients With Lafora Disease

This study will test the safety and efficacy of multiple doses of ION283 administered as intrathecal (IT) injections by lumbar puncture (LP). All subjects will…

United States10 participantsStarted 2024-12-03

Treatment: ION283

All recent trials (4 shown)

AVAILABLENot Applicable

NCT05930223

Intravenous VAL-1221 Lafora Expanded Access Protocol

Only qualified physicians treating a Lafora Disease patient may request VAL-1221 Expanded Access treatment under the Parasail Lafora Expanded Access Protocol (L…

Location not specified

Treatment: VAL-1221

CompletedNot Applicable

NCT03876522

Natural History and Functional Status Study of Patients With Lafora Disease

A natural history and functional status study to characterize the clinical disease course in Lafora disease patients using standardized, quantitative evaluation…

United States, Italy, Spain33 participantsStarted 2019-01-09

CompletedNot Applicable

NCT00007124

Lafora Disease

Trial phase breakdown

Trial status

Actively recruiting — 1 trial

A Safety and Efficacy of Intrathecally Administered ION283 in Patients With Lafora Disease

All recent trials (4 shown)

Intravenous VAL-1221 Lafora Expanded Access Protocol

Natural History and Functional Status Study of Patients With Lafora Disease

Ketogenic Diet in Lafora Disease

Trial phase breakdown

Trial status

Actively recruiting — 1 trial

A Safety and Efficacy of Intrathecally Administered ION283 in Patients With Lafora Disease

All recent trials (4 shown)

Intravenous VAL-1221 Lafora Expanded Access Protocol

Natural History and Functional Status Study of Patients With Lafora Disease

Ketogenic Diet in Lafora Disease