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Inherited Retinal Dystrophy Due to RPE65 Mutations
Clinical trial pipeline · Data from ClinicalTrials.gov
See which Inherited Retinal Dystrophy Due to RPE65 Mutations trials may be worth asking aboutClinical trial pipeline · Data from ClinicalTrials.gov
See which Inherited Retinal Dystrophy Due to RPE65 Mutations trials may be worth asking aboutNorth America
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The study is a Phase 3, open-label, randomized controlled trial of gene therapy intervention by subretinal administration of AAV2-hRPE65v2 (voretigene neparvove…
Multi-site, non-randomized, observational study, for up to 15 years after subretinal AAV2-hRPE65v2 administration for each subject. The study is a non-intervent…
Rationale: In preparation for treatment with gene therapy, this study is being conducted in order to investigate the natural history of Inherited Retinal Dystr…
The purpose of this study is: * to evaluate the safety of oral QLT091001 * to evaluate whether 7-day treatment with oral QLT091001 can improve visual function…